Les médicaments marqués en jaune ont la description texte.
- CERDELGA /capsule/: eliglustat (84)
- DOJOLVI /liquide/: triheptanoin (100)
- GALAFOLD /capsule/: migalastat (123)
- GIVLAARI /solution/: givosiran (189)
- KUVAN /comprimé/: sapropterin dihydrochloride (100)
- KUVAN /poudre/: sapropterin dihydrochloride (100)
- KUVAN /poudre/: sapropterin dihydrochloride (500)
- MAR-TRIENTINE /capsule/: trientine hydrochloride (250)
- MDK-NITISINONE /capsule/: nitisinone (10)
- MDK-NITISINONE /capsule/: nitisinone (2)
- MDK-NITISINONE /capsule/: nitisinone (5)
- NITISINONE TABLETS /comprimé/: nitisinone (2)
- NITISINONE TABLETS /comprimé/: nitisinone (5)
- NITISINONE TABLETS /comprimé/: nitisinone (10)
- ORFADIN /capsule/: nitisinone (5)
- ORFADIN /capsule/: nitisinone (20)
- ORFADIN /suspension/: nitisinone (4)
- ORFADIN /capsule/: nitisinone (2)
- ORFADIN /capsule/: nitisinone (10)
- OXLUMO /solution/: lumasiran (94.5)
- PHEBURANE /granules/: sodium phenylbutyrate (483)
- RAVICTI /liquide/: glycerol phenylbutyrate (1.1)
- REDDY-SAPROPTERIN /poudre pour solution/: sapropterin dihydrochloride (100)
- REDDY-SAPROPTERIN /poudre pour solution/: sapropterin dihydrochloride (500)
- REVESTIVE /trousse, poudre pour solution/: teduglutide (5)
- SANDOZ MIGLUSTAT /capsule/: miglustat (100)
- SIALOR /comprimé/: anethole trithione (25.0)
- WAYMADE-TRIENTINE /capsule/: trientine hydrochloride (250)
- XERMELO /comprimé/: telotristat ethyl (250)
- ZAVESCA /capsule/: miglustat (100)
30 médicaments correspondent à la recherche.