Les médicaments marqués en jaune ont la description texte.
- ALDURAZYME /solution/: laronidase (0.58)
- BRINEURA /solution/: cerliponase alfa (150)
- CARBAGLU /comprimé pour suspension/: carglumic acid (200)
- CARNITOR /solution/: levocarnitine (200)
- CARNITOR /solution/: levocarnitine (100)
- CARNITOR /comprimé/: levocarnitine (330)
- CERDELGA /capsule/: eliglustat (84)
- CEREZYME /poudre pour solution/: imiglucerase (400)
- CYSTADANE /poudre pour solution/: betaine (1)
- DOJOLVI /liquide/: triheptanoin (100)
- ELAPRASE /solution/: idursulfase (2)
- ELELYSO /poudre pour solution/: taliglucerase alfa (200)
- FABRAZYME /poudre pour solution/: agalsidase beta (5)
- FABRAZYME /poudre pour solution/: agalsidase beta (35)
- GALAFOLD /capsule/: migalastat (123)
- GIVLAARI /solution/: givosiran (189)
- KANUMA /solution/: sebelipase alfa (2)
- KUVAN /comprimé/: sapropterin dihydrochloride (100)
- KUVAN /poudre/: sapropterin dihydrochloride (100)
- KUVAN /poudre/: sapropterin dihydrochloride (500)
- MAR-TRIENTINE /capsule/: trientine hydrochloride (250)
- MDK-NITISINONE /capsule/: nitisinone (10)
- MDK-NITISINONE /capsule/: nitisinone (2)
- MDK-NITISINONE /capsule/: nitisinone (5)
- MYOZYME /poudre pour solution/: alglucosidase alfa (50)
- NAGLAZYME /solution/: galsulfase (1)
- NEXVIAZYME /poudre pour solution/: avalglucosidase alfa (100)
- NITISINONE TABLETS /comprimé/: nitisinone (2)
- NITISINONE TABLETS /comprimé/: nitisinone (5)
- NITISINONE TABLETS /comprimé/: nitisinone (10)
- ODAN LEVOCARNITINE /solution/: levocarnitine (100)
- ORFADIN /suspension/: nitisinone (4)
- ORFADIN /capsule/: nitisinone (2)
- ORFADIN /capsule/: nitisinone (10)
- ORFADIN /capsule/: nitisinone (5)
- ORFADIN /capsule/: nitisinone (20)
- OXLUMO /solution/: lumasiran (94.5)
- PALYNZIQ /solution/: pegvaliase (2.5)
- PALYNZIQ /solution/: pegvaliase (10)
- PALYNZIQ /solution/: pegvaliase (20)
- PHEBURANE /granules/: sodium phenylbutyrate (483)
- PROCYSBI /capsule (à libération retardée)/: cysteamine (25)
- PROCYSBI /capsule (à libération retardée)/: cysteamine (75)
- RAVICTI /liquide/: glycerol phenylbutyrate (1.1)
- REPLAGAL /solution/: agalsidase alfa (1)
- REVESTIVE /trousse, poudre pour solution/: teduglutide (5)
- SANDOZ MIGLUSTAT /capsule/: miglustat (100)
- SIALOR /comprimé/: anethole trithione (25.0)
- STRENSIQ /solution/: asfotase alfa (40)
- STRENSIQ /solution/: asfotase alfa (100)
- STRENSIQ /solution/: asfotase alfa (40)
- STRENSIQ /solution/: asfotase alfa (40)
- VIMIZIM /solution/: elosulfase alfa (1)
- VPRIV /poudre pour solution/: velaglucerase alfa (400)
- WAYMADE-TRIENTINE /capsule/: trientine hydrochloride (250)
- XERMELO /comprimé/: telotristat ethyl (250)
- ZAVESCA /capsule/: miglustat (100)
57 médicaments correspondent à la recherche.