Drugs marked in yellow have text description.

• ALDURAZYME /solution/: laronidase (0.58)
• BRINEURA /solution/: cerliponase alfa (150)
• CARBAGLU /tablet for suspension/: carglumic acid (200)
• CARNITOR /solution/: levocarnitine (200)
• CARNITOR /solution/: levocarnitine (100)
• CARNITOR /tablet/: levocarnitine (330)
• CERDELGA /capsule/: eliglustat (84)
• CEREZYME /powder for solution/: imiglucerase (400)
• CYSTADANE /powder for solution/: betaine (1)
• DOJOLVI /liquid/: triheptanoin (100)
• ELAPRASE /solution/: idursulfase (2)
• ELELYSO /powder for solution/: taliglucerase alfa (200)
• FABRAZYME /powder for solution/: agalsidase beta (5)
• FABRAZYME /powder for solution/: agalsidase beta (35)
• GALAFOLD /capsule/: migalastat (123)
• GIVLAARI /solution/: givosiran (189)
• KANUMA /solution/: sebelipase alfa (2)
• KUVAN /tablet/: sapropterin dihydrochloride (100)
• KUVAN /powder/: sapropterin dihydrochloride (100)
• KUVAN /powder/: sapropterin dihydrochloride (500)
• MAR-TRIENTINE /capsule/: trientine hydrochloride (250)
• MDK-NITISINONE /capsule/: nitisinone (10)
• MDK-NITISINONE /capsule/: nitisinone (2)
• MDK-NITISINONE /capsule/: nitisinone (5)
• MYOZYME /powder for solution/: alglucosidase alfa (50)
• NAGLAZYME /solution/: galsulfase (1)
• NEXVIAZYME /powder for solution/: avalglucosidase alfa (100)
• NITISINONE TABLETS /tablet/: nitisinone (2)
• NITISINONE TABLETS /tablet/: nitisinone (5)
• NITISINONE TABLETS /tablet/: nitisinone (10)
• ODAN LEVOCARNITINE /solution/: levocarnitine (100)
• ORFADIN /capsule/: nitisinone (5)
• ORFADIN /capsule/: nitisinone (20)
• ORFADIN /suspension/: nitisinone (4)
• ORFADIN /capsule/: nitisinone (2)
• ORFADIN /capsule/: nitisinone (10)
• OXLUMO /solution/: lumasiran (94.5)
• PALYNZIQ /solution/: pegvaliase (2.5)
• PALYNZIQ /solution/: pegvaliase (10)
• PALYNZIQ /solution/: pegvaliase (20)
• PHEBURANE /granules/: sodium phenylbutyrate (483)
• PROCYSBI /capsule (delayed release)/: cysteamine (25)
• PROCYSBI /capsule (delayed release)/: cysteamine (75)
• RAVICTI /liquid/: glycerol phenylbutyrate (1.1)
• REDDY-SAPROPTERIN /powder for solution/: sapropterin dihydrochloride (100)
• REDDY-SAPROPTERIN /powder for solution/: sapropterin dihydrochloride (500)
• REPLAGAL /solution/: agalsidase alfa (1)
• REVESTIVE /kit, powder for solution/: teduglutide (5)
• SANDOZ MIGLUSTAT /capsule/: miglustat (100)
• SIALOR /tablet/: anethole trithione (25.0)
• STRENSIQ /solution/: asfotase alfa (40)
• STRENSIQ /solution/: asfotase alfa (40)
• STRENSIQ /solution/: asfotase alfa (40)
• STRENSIQ /solution/: asfotase alfa (100)
• VIMIZIM /solution/: elosulfase alfa (1)
• VPRIV /powder for solution/: velaglucerase alfa (400)
• WAYMADE-TRIENTINE /capsule/: trientine hydrochloride (250)
• XERMELO /tablet/: telotristat ethyl (250)
• ZAVESCA /capsule/: miglustat (100)

Found 59 matches.